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Orphan Drugs: Research and Reviews ceased publishing in September 2018. All articles that have been published in Orphan Drugs: Research and Reviews will continue to be available on the Dove Press site, and will be securely archived with CLOCKSS.
Orphan Drugs: Research and Reviews
ISSN: 2230-6161
- View all (36)
- Volume 7, 2017 (4)
- Volume 6, 2016 (1)
- Volume 5, 2015 (12)
- Volume 4, 2014 (11)
- Volume 3, 2013 (3)
- Volume 2, 2012 (4)
- Volume 1, 2011 (1)
Journal Articles:
- 36 records -
Orphan drugs for the treatment of aspergillosis: focus on isavuconazole
Jacobs SE, Petraitis V, Small CB, Walsh TJ
Orphan Drugs: Research and Reviews 2017, 7:37-46
Published Date: 3 May 2017
Nitisinone: a review
Aktuglu-Zeybek AC, Zubarioglu T
Orphan Drugs: Research and Reviews 2017, 7:25-35
Published Date: 31 January 2017
Spotlight on anagrelide hydrochloride for the treatment of essential thrombocythemia
Sarma A, Mclornan DP, Harrison CN
Orphan Drugs: Research and Reviews 2017, 7:11-23
Published Date: 31 January 2017
Pompe disease: clinical perspectives
Cabello JF, Marsden D
Orphan Drugs: Research and Reviews 2017, 7:1-10
Published Date: 28 December 2016
Adverse events reported for hereditary angioedema medications: a retrospective study of spontaneous reports submitted to the EudraVigilance database, 2007-2013
Aagaard L, Bygum A
Orphan Drugs: Research and Reviews 2016, 6:1-8
Published Date: 3 May 2016
Denosumab in the treatment of hypercalcemia secondary to malignancy
Dalkin AC, Rosner MH
Orphan Drugs: Research and Reviews 2015, 5:113-121
Published Date: 23 November 2015
Orphan drugs for sickle vaso-occlusion: dawn of a new era of targeted treatment
Dampier C
Orphan Drugs: Research and Reviews 2015, 5:99-112
Published Date: 2 November 2015
Orphan drugs in development for primary biliary cirrhosis: challenges and progress
Ali AH, Byrne TJ, Lindor KD
Orphan Drugs: Research and Reviews 2015, 5:83-97
Published Date: 10 September 2015
Paroxysmal nocturnal hemoglobinuria: new concepts in pathophysiology and treatment
Weitz IC
Orphan Drugs: Research and Reviews 2015, 5:75-81
Published Date: 1 September 2015
The efficacy and safety of adalimumab in ocular inflammatory disease
Arcinue CA, Durrani K, Artornsombudh P, Radwan A, Parikh R, Suelves AM, Siddique SS, Chang I, Preble JM, Foster CS
Orphan Drugs: Research and Reviews 2015, 5:69-74
Published Date: 31 August 2015
Profile of lumacaftor/ivacaftor combination: potential in the treatment of cystic fibrosis
Arends AM, Pettit RS
Orphan Drugs: Research and Reviews 2015, 5:61-68
Published Date: 14 August 2015
Drugs in development and dietary approach for Duchenne muscular dystrophy
Angelini C, Tasca E
Orphan Drugs: Research and Reviews 2015, 5:51-60
Published Date: 11 August 2015
Fahr's disease: current perspectives
Tai XY, Batla A
Orphan Drugs: Research and Reviews 2015, 5:43-49
Published Date: 16 July 2015
Orphan drugs in development for long-chain fatty acid oxidation disorders: challenges and progress
Sun A, Merritt II JL
Orphan Drugs: Research and Reviews 2015, 5:33-41
Published Date: 28 April 2015
Amyotrophic lateral sclerosis: clinical perspectives
Haringer VC, Gibson SB
Orphan Drugs: Research and Reviews 2015, 5:19-31
Published Date: 15 April 2015
Update on the challenges of treating trigeminal neuralgia
Obermann M
Orphan Drugs: Research and Reviews 2015, 5:11-17
Published Date: 10 April 2015
Orphan drugs in development for Huntington's disease: challenges and progress
Burgunder JM
Orphan Drugs: Research and Reviews 2015, 5:1-9
Published Date: 12 February 2015
Optimal management of interstitial lung disease associated with dermatomyositis/polymyositis: lessons from the Japanese experience
Kurasawa K, Arai S
Orphan Drugs: Research and Reviews 2014, 4:93-107
Published Date: 21 November 2014
Orphan drugs in glioblastoma multiforme: a review
Lassen U, Mau-Sørensen M, Poulsen HS
Orphan Drugs: Research and Reviews 2014, 4:83-91
Published Date: 14 November 2014
New treatments in development for Pseudomonas aeruginosa infections in the lungs of individuals with cystic fibrosis
Akhand SS, Pettit RS, Gardner TE, Anderson GG
Orphan Drugs: Research and Reviews 2014, 4:71-81
Published Date: 24 October 2014
Orphan drugs in development for urea cycle disorders: current perspectives
Häberle J, McCandless SE
Orphan Drugs: Research and Reviews 2014, 4:63-70
Published Date: 30 September 2014
Angiogenesis inhibitors in gastric cancer
McCarthy T, O'Neil BH
Orphan Drugs: Research and Reviews 2014, 4:55-61
Published Date: 14 July 2014
An update on gene therapy for the treatment of lipoprotein lipase deficiency
Libby AE, Wang H
Orphan Drugs: Research and Reviews 2014, 4:47-54
Published Date: 15 May 2014
Access to cross-border health care services for patients with rare diseases in the European Union
Aagaard L, Kristensen K
Orphan Drugs: Research and Reviews 2014, 4:39-45
Published Date: 11 April 2014
Stiripentol for the treatment of Dravet syndrome
Chiron C
Orphan Drugs: Research and Reviews 2014, 4:29-38
Published Date: 2 April 2014
A 30-year retrospective: National Organization for Rare Disorders, the Orphan Drug Act, and the role of rare disease patient advocacy groups
Dunkle M
Orphan Drugs: Research and Reviews 2014, 4:19-27
Published Date: 17 February 2014
Profile of aminopyridines for Lambert–Eaton myasthenic syndrome
Maddison P, Keogh MJ, Sedehizadeh S
Orphan Drugs: Research and Reviews 2014, 4:11-18
Published Date: 20 January 2014
Post-marketing access to orphan drugs: a critical analysis of health technology assessment and reimbursement decision-making considerations
Iskrov G, Stefanov R
Orphan Drugs: Research and Reviews 2014, 4:1-9
Published Date: 9 January 2014
Do ultra-orphan medicinal products warrant ultra-high prices? A review
Picavet E, Cassiman D, Simoens S
Orphan Drugs: Research and Reviews 2013, 3:23-31
Published Date: 24 June 2013
Tipifarnib and farnesyltransferase inhibitors in the treatment of inflammatory breast cancer: is the story over? A review
Dehghan-Paz I, Il’yasova D, van Golen KL, Usha L
Orphan Drugs: Research and Reviews 2013, 3:11-21
Published Date: 15 May 2013
Current management options for tyrosinemia
El-Shabrawi MH, Kamal NM
Orphan Drugs: Research and Reviews 2013, 3:1-9
Published Date: 1 March 2013
Wilson’s disease: a review of treatment options with a focus on zinc therapy
Hui J, Tang NL
Orphan Drugs: Research and Reviews 2012, 2:35-45
Published Date: 11 October 2012
Betaine treatment of cystathionine β-synthase-deficient homocystinuria; does it work and can it be improved?
Maclean KN
Orphan Drugs: Research and Reviews 2012, 2:23-33
Published Date: 28 September 2012
Prussian blue as an antidote for radioactive thallium and cesium poisoning
Altagracia-Martinez M, Kravzov-Jinich J, Martínez-Núñez JM, Ríos-Castañeda C, López-Naranjo F
Orphan Drugs: Research and Reviews 2012, 2:13-21
Published Date: 8 June 2012
Potential role of enzastaurin in the treatment of patients with relapsed or refractory advanced cutaneous T-cell lymphomas: a review
Katz DA, Plate JM, Nathan S, Usha L
Orphan Drugs: Research and Reviews 2012, 2:1-12
Published Date: 22 June 2012
Medical treatment of rare diseases must be put on the agenda
Aagaard L
Orphan Drugs: Research and Reviews 2011, 1:1-2
Published Date: 23 September 2011