Medical treatment of rare diseases must be put on the agenda
Faculty of Pharmaceutical Sciences, University of Copenhagen, University of Copenhagen, Copenhagen, Denmark
The development of medicines for the treatment of rare diseases is important to many, including both patients and prescribers, but has traditionally been of minor interest to the pharmaceutical industry due to the often low number of patients with a rare disease. Politicians and regulators have recently acknowledged this problem, and favorable licensing conditions are now offered to pharmaceutical companies developing new medications for rare diseases to make these products more accessible.
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